Leber congenital amaurosis (LCA) is a rare inherited eye disorder. This is one the most common cause of inherited eyesight loss in younger population. Dysfunctioning of the retinal pigment epithelium is responsible for the gradual onset of LCA. In this regard, gene therapy has succeeded in finding the answer. The therapy includes injecting healthy genes that will produce a protein responsible for retaining a normal eye vision has been considered by the FDA panel for the approval.
Although the therapy needs well-established data and it will take years before it hits the Indian market, the article mainly highlights the breakthrough in the LCA treatment. Leber congenital amaurosis (LCA) is rare eye disorder that mainly affects the retina. LCA is characterized by photophobia, involuntary eye movements (nystagmus), and extreme farsightedness (hyperopia). In this disease, pupils do not…
