Hemophilia is a genetic disorder in which the bleeding and clotting times are prolonged. A deficiency or absence of clotting factors is the primary cause of this genetic presentation. The treatment for hemophilia mainly focuses on preventing bleeds clinically or at home. On this World Hemophilia Day , let’s take a look at the gene therapies available for treating hemophilia.
The theme of this year is “Access for All: Prevention of bleeds as the global standard of care.” Gene therapy is a one-time treatment wherein a gene is introduced to liver cells using harmless viral vectors that stimulate the clotting factors and stop spontaneous bleeding episodes. Gene therapies have been shown to effectively reduce the rate of bleeding in patients with hemophilia, thus giving us hope to improve the quality of life of these patients. Swipe through the carousel slides to know about the gene…
